Update from Roche/Genentech on RG6042 Huntington’s disease global development program: Two clinical studies to begin by end of 2018

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Over the past months we and our partner Ionis Pharmaceuticals have been heavily engaged with communities around the world (patient groups, medical professionals, Health Authorities and payers) to collaborate and build the RG6042 global development programme and upcoming studies. We are eager for RG6042 to advance into further clinical development. In addition, as announced last month, the European Medicines Agency granted RG6042 PRIME (“PRIority MEdicine”) designation, which provides promising medicines enhanced interactions with the agency and the potential for accelerated evaluation.

READ THE FULL PRESS RELEASE AND LEARN ABOUT THE NEXT STEPS, ONGOING AND UPCOMING CLINICAL STUDIES FOR THE GLOBAL RG6042 DEVELOPMENT PROGRAM.

Exciting news from Ionis Pharmaceuticals! Potentially faster approval for HTTRx!

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Ionis Pharmaceuticals, Inc. announced that the European Medicines Agency (EMA) has granted Priority Medicines (PRIME) designation to IONIS-HTTRx for the treatment of people with Huntington's disease (HD). This PRIME designation means this potentially disease-modifying drug for people with Huntington's disease to regulatory approval faster. This is exciting news! Read the full press release.

Powerful new approach helps understand molecular alterations in neurological disease

 CREDIT: BAYLOR COLLEGE OF MEDICINE

CREDIT: BAYLOR COLLEGE OF MEDICINE

Neurological diseases are typically associated with a multitude of molecular changes. But out of these thousands of changes in gene expression, which ones are actually driving the disease? Read full story.

Funding for this work was provided, in part, by a grant from the Hereditary Disease Foundation.

SAVE THE DATE - Jackie's Walk 4 HD, October 14, 2018

Jackie's Walk for HD 2018 will be held October 14th, at Glen Island Park in New Rochelle, NY with the Hereditary Disease Foundation (HDF). HDF was the first organization funding research and continues to inspire innovation in the field of Huntington's disease research. We are so happy to run this event as part of HDF’s 50th Anniversary celebration.

We hope that you will join us in this day of fun and celebration as the latest research for HD is so promising!

Click for more details.